Pharmacokinetics and pharmacodynamics of PTC518, an oral huntingtin lowering splicing modifier: A first-in-human study : British Journal of Clinical Pharmacolog

an Gao 1 | Anuradha Bhattacharyya 1 | Brian Beers 1 | Diksha Kaushik 1 | Amy-Lee Bredlau 1 | Allan Kristensen 1 | Khalid Abd-Elaziz 2 | Richard Grant 1 | Lee Golden 1 | Ronald Kong2024-09-032024-09-032024-09-03http://98.70.32.231:4000/handle/123456789/1334Pharmacokinetics and pharmacodynamics of PTC518, an oral huntingtin lowering splicing modifier: A first-in-human study : British Journal of Clinical PharmacologArticle